Latest Updates
Latest Updates
Gene Therapy Research Update – August 2026 Steps Closer to a Treatment for Friedreich’s Ataxia (FA)
Gene Therapy Research Update - August 2026 Steps Closer to a Treatment for Friedreich's…
In vivo studies have started
This video shows part of the AAV virus production workflow in the lab, where the virus is…
Update from the lab
This video shows part of the AAV virus production workflow in the lab, where the virus is…
An evening of laughter in support of FA
All proceeds go directly to CureFAchildren’s gene therapy program at UTSW - to create…
We’ve reached Phase 2 – thanks to you!
We now move forward with cell testing and AAV production. But the fight continues.