New groundbreaking gene therapy program with one goal: to save this generation - and with your support, we will.
This is a nonprofit led by parents, fighting to save lives. Every donation goes directly to the research — and nowhere else.
Two years ago, both our sons were diagnosed with Friedreich’s Ataxia (FA). A brutal disease that slowly takes everything away–their balance, their mobility, and eventually their heartbeat
But today there is hope – a revolutionary gene thearapy program is underway – and with your help, we can bring it to life in record time.
What´s happening now
Research has already begun. Feb-25
We are working with worldleading gene therapy pioneers.
We are racing against time
Every donation fuels the next breakthrough.
How can you help:
Donate now – every amount matters.
Share our story – Help us reach more hearts.
Be part of saving lives – The most beautiful act you can make.
Why can we succeed:
We are partnering with scientists who have already taken eight rare diseases to clinical trials, and more are on the way. This is real. This is happening now.
🧬 Join Dr. Steven Gray and leading pediatric neurologists in a powerful conversation on gene therapy, innovation, and hope. 🎥 Watch the reel and learn how research is becoming reality.
Complete Work towards Proof of Concept (POC)
- Codon-optimized FXN gene ordered and inserted
- into plasmid
- Cloning and DNA kit, cloning succeeded on second attempt (one correct colony verified)
- DNA synthesis and cloning
- Sequencing confirmed correct gene structure
- Virus production (AAV vector, viruses being produced)
POC: timeline: If everything goes according to plan, about 1 year or slightly more
Milestones Towards a Cure
Milestones Towards a Cure
Make a difference today
Every donation helps us fight for a future without Friedreich’s Ataxia.
You’ll be supporting cutting-edge gene therapy research and giving children like Tom and Lev the chance to walk, grow, and live full lives.
SWISH: +123 291 07 27
Bankgiro: 893-5744
Corporate & Large Donations
Are you a company, organisation, or private donor interested in supporting our mission?
Contact us directly to discuss partnership or sponsorship
CUREFACHILDREN
Org nr: 802551-2255
Contact us directly:
zardasht@curefachildren.com
+46 73 655 38 37
Thank you, your generosity enables us to carry out our mission!
Contact Form:
You can also fill out our contact form below and we will be in touch shortly.
