“A new, groundbreaking gene therapy program – our goal is to save this generation in record time. But we need your support.”
“For nearly two years, our world has been turned upside down. Our wonderful children were diagnosed with the rare disease Friedreich’s Ataxia (FA). This brutal condition slowly takes everything away–their balance, their mobility, and eventually their heartbeat.”
But there is hope–a solution is within reach.
With your support, we can make it a reality.
Currently, there is no cure for FA. However, gene therapy offers a revolutionary approach by delivering a functional copy of the FXN gene directly into affected cells, potentially stopping or even reversing the disease’s progression. FA is a strong candidate for this breakthrough and together with UTSW we have started a research program specifically for children affected by FA.
“Our program is driven by parents who refuse to accept the status quo – who believe in saving lives over maximizing profit, who partner with the best minds in science, and who will stop at nothing to deliver a life-saving gene therapy for Friedreich’s ataxia in record time.”
Your generosity enables us to carry out our mission.
Support us by contributing a gift.
Du kan också stödja oss via SWISH: +123 343 55 52
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